Somatic Cell Gene Editing

Advanced Therapies Week 2027
2027-01-18 - 2027-01-21
Advanced Therapies Week is a premier biotech partnering event in the United States, bringing together leaders in research, therapeutic development, and advanced manufacturing.
San Diego, CA
Learn more at: https://www.phacilitate.com/advanced-therapies-week

Safety, Translation, and Real-World Implementation of AAV and LNP Gene Therapies
2026-11-20 07:30 - 16:35 (America/Chicago)
Join the American Society of Gene & Cell Therapy (ASGCT) and the Clinical In Vivo Gene Therapy (CIGT) group at the Children’s Hospital of Philadelphia (CHOP) alongside fellow clinicians and translational researchers for this focused, one-day, CME-accredited* program. This event examines the safe translation and real-world implementation of AAV and LNP in vivo gene therapies within modern clinical practice.
Philadelphia, PA
Learn more at: https://www.asgct.org/events-meetings/safety-translation-and-real-world-implementation-of-aav-and-lnp-gene-therapies

NORD Rare Diseases and Orphan Products Breakthrough Summit 2026
2026-10-25 - 2026-10-27
Shape the future of rare disease treatments, research and policy at the NORD® Rare Diseases and Orphan Products Breakthrough Summit.® Together, we can advance innovation for the more than 30 million Americans – and more than 400 million people worldwide – with rare diseases!
Washington D.C.
Learn more at: https://nordsummit.org/

7th Annual Genome Editing Therapeutics Summit
2026-09-28 - 2026-09-30
Spearheading Safety, Clinical Efficacy and Regulatory Compliance Using Advanced Genetic Engineering & Novel Delivery Platforms to Shape the Next Era of Genome Editing.
Boston, MA
Learn more: https://genome-editing-therapeutics-summit.com/

Gene Editing and RNA Technologies (GEAR)
2026-09-15 - 2026-09-17
The program features cutting edge research in CRISPR and emerging gene editing tools, RNA interference, mRNA platforms, and novel delivery technologies. Attendees will explore translational challenges, manufacturing, and regulatory considerations, and ethical implications shaping the field.
Featured speakers include SCGE researchers David Liu and Benjamin Kleinstiver.
Boston, MA
Learn more at https://www.aiche.org/sbe/conferences/gene-editing-rna-technologies-gear/2026

2026 Policy Summit
2026-09-14
Cell and gene therapies are transforming healthcare, but their full potential depends on a supportive policy landscape. Join leading policymakers, industry executives, and scientific stakeholders to discuss the most pressing issues and collaborate on innovative solutions at this dynamic, one-day event in Washington, D.C.
Learn more at https://www.asgct.org/events-meetings/2026-policy-summit

ASGCT Graduate Medical Education Bootcamp in Cell and Gene Therapy
2026-08-21
This focused, one-day program is designed to prepare the next generation of clinicians to safely and effectively integrate cell and gene therapies (CGT) into patient care. Hosted at Nationwide Children’s Hospital, this structured, clinically-grounded program bridges the gap between scientific innovation and bedside implementation.
Learn more at https://www.asgct.org/events-meetings/asgct-graduate-medical-education-bootcamp-in-cell-and-gene-therapy

Genome Engineering: Research and Applications
2026-07-06 - 2026-07-09
This year’s program will present findings on genome editing outcomes, pre-clinical translation of editing technologies, in vivo delivery of genome editors, and clinical trials of genome editors.
Many SCGE researchers are presenting at this event, including Ben Kleinstiver, David Liu, Shengdar Tsai, Bill Peranteau, Ben Devernman, Sonia Vallabh, and Kiran Musunuru.
Find more info and register at https://events.faseb.org/event/genome-engineering/summary
Porto, Portugal

3rd Global Cell & Gene Therapy Summit
2026-07-06 - 2026-07-08
This three-day conference aims to bring together a global audience to discuss and exchange ideas on the origins, development, clinical applications, and translational science of cell and gene therapy.
Boston, MA

Global Harmonization: Insights from the ICH CGT Discussion Group
2026-06-24 11:00 - 12:00
The global development of cell and gene therapies is accelerating rapidly, yet divergent regulatory expectations across regions remain a significant barrier for developers and patient access. To address these challenges, the International Council for Harmonization (ICH) established the Cell & Gene Therapy Discussion Group (CGT DG). This free, expert-led webinar explores the group’s mission to map global regulatory frameworks, identify critical areas of divergence, and propose a strategic roadmap for international harmonization.
Virtual webinar
Learn more: https://www.asgct.org/events-meetings/global-harmonization-insights-from-the-ich-cgt-discussion-group

CRISPR 2026
2026-06-10 - 2026-06-12
The CRISPR meeting has a distinguished history. It was the first meeting focusing on the emerging topic of CRISPR-Cas. It was at this podium that researchers shared their groundbreaking discoveries on CRISPR-Cas and witnessed the birth of the genome editing revolution.
SCGE researcher Benjamin Kleinstiver is scheduled to be speaking at the event.
Omni New Haven Hotel at Yale
Learn more: https://web.cvent.com/event/ac20b6f2-79c9-4ab7-87ae-f650579f4e42/summary?environment=P2

World Orphan Drug Congress USA 2026
2026-06-09 - 2026-06-11
The World Orphan Drug Congress USA brings together the leading pharmaceutical and biotechnology companies, government and regulators, patient advocates, payers, investors, and solution providers – all who all depend on our event to convene and brainstorm ways to advance.
Boston, MA

Breakthroughs in Cell & Gene Therapy 2026
2026-05-15 08:00 - 17:00
For the third year, ASGCT brings Breakthroughs in Cell & Gene Therapy to a new region, and this time, we’re heading to Music City! Join us November 12-13 at the Gaylord Opryland Resort in Nashville for our most expansive program yet: three concurrent tracks designed for the scientists, clinicians, and industry leaders shaping what’s next in the field.
Learn more at: https://www.asgct.org/events-meetings/breakthroughs-in-cell-gene-therapy

ASGCT 2026 Annual Meeting
2026-05-12 - 2026-05-16
Boston, MA or Virtual
https://annualmeeting.asgct.org/

ISCT 2026
2026-05-06 - 2026-05-09
International Society for Cell & Gene Therapy 2026 Annual Meeting
Dublin, Ireland
https://www.isctglobal.org/meetings/annual-meeting/isct-2026-dublin

2nd Annual Gene Therapy Symposium
2026-04-24 - 2026-04-25
The 2nd Annual Gene Therapy Symposium brings together leading scientists, clinicians, and industry innovators shaping the future of genetic medicine. Our speakers represent a diverse cross-section of expertise across research, clinical translation, regulatory science, and biotechnology.

SCGE researcher Becca Ahrens-Nicklas will be speaking at the event.

Columbus, OH

Learn more at https://web.cvent.com/event/2c97ab51-3da3-46df-abb4-544a428dcfa6/summary

NORD® Rare Disease Scientific Symposium 2026
2026-04-14 - 2026-04-15
The NORD® Rare Disease Scientific Symposium is bringing together a dynamic community of researchers, clinicians, industry leaders, and advocates to spark the conversations and connections that drive science forward.
This immersive, 1.5 day event is designed to push boundaries and bridge gaps across the rare disease landscape. Through engaging case studies, interactive panel discussions, and extended audience Q&A, participants will explore critical topics such as:

Innovative Study Designs and Methods for Rare Disease Research
Approaches to Address the Challenges of Small Trial Enrollment and Disease Heterogeneity
Successes and Challenges of Global Clinical Trials
Using Alternative and Real-World Data for Rare Disease Research
Multi-Stakeholder Collaboration in Research
Strategies for Earlier Pediatric Inclusion in Clinical Trials

Learn more at: https://nordscience.org/

PPQ Readiness: What to Know Before Starting a PPQ Campaign
2026-04-08 11:00 - 12:00
Process Performance Qualification (PPQ) verifies that a therapy’s manufacturing process consistently produces high-quality doses; regulators rely on the results before allowing wider use. This free webinar will define what must be in place before a campaign launch, outline the activities that precede PPQ, and highlight common gaps and pitfalls, along with practical mitigation steps.
Learn more at https://www.asgct.org/events-meetings/ppq-readiness-what-to-know-before-starting-a-ppq-campaign

Molecular Therapy Presents: Lipid Nanoparticles for Gene and Cell Therapy
2026-03-25 10:00 - 11:00
Lipid nanoparticles (LNPs) have emerged as promising vehicles for delivering therapeutic payloads for cell and gene therapy. They offer several advantages, such as biocompatibility, low immunogenicity, and the ability to encapsulate a wide range of cargoes. From the development of mRNA vaccines to the targeted delivery of gene editing tools and RNA interference therapeutics, LNPs are driving transformative breakthroughs in treating a myriad of diseases, including cancers, genetic disorders, and infectious diseases.
This free webinar will explore the complex interplay between advanced nanotechnology and biomedical innovation, focusing on the transformative potential of LNPs in developing precise and effective therapeutic interventions.
Learn more at https://www.asgct.org/events-meetings/molecular-therapy-presents-lipid-nanoparticles-for-gene-and-cell-therapy

9th Annual Gene Therapy Development Summit
2026-03-24 - 2026-03-26
The 9th Gene Therapy Development Summit returns to Boston as the meeting point for this community. Join 100+ leading voices from the likes of Bayer, Astellas Pharmaceuticals, REGENXBIO, Ocugen, AskBio, CureDuchenne Ventures, and more to come together to share ideas, restore confidence, and chart a sustainable path forward for gene therapy. Connect with your peers in pre-clinical development, manufacturing, analytical development, clinical operations, and regulatory affairs for an unrivalled learning and networking opportunity across the end-to-end of gene therapy development.
Boston, MA

Empowering Patients 2026: A Cell and Gene Therapies Summit
2026-03-11 - 2026-03-12
This free, virtual summit from ASGCT will bring together patients, caregivers, advocates, researchers, and industry leaders for two dynamic half-days of learning the latest insights in cell and gene therapy.
Hear from SCGE researchers Steve Gray and Kiran Musunuru at the event.

Rare Disease Day at NIH
2026-02-27 08:00 - 16:00
Rare Disease Day at NIH aims to raise awareness about rare diseases, the people they affect and NIH collaborations that address scientific challenges and advance research for new treatments.
The event will be held at NIH Main Campus (Natcher Conference Center), and there will also be a virtual livestream, with the event archived for replay afterward. The event is free and open to the public.
More info at: https://ncats.nih.gov/news-events/events/rdd

Public Meeting: FDA Rare Disease Day 2026
2026-02-23 08:00 - 15:00
FDA will host Rare Disease Day, a virtual public meeting, on Monday, February 23, 2026 in global observance of Rare Disease Week. The theme is: “Moving Forward. Looking Ahead. An Event for Patients.” The goal of this year’s Rare Disease Day is to explore ways to engage and collaborate with patients and their communities to support and accelerate the development of medical products for rare diseases. We want patients to connect with FDA and stay involved with our outreach and engagement programs to ensure the patient voice informs medical product development and regulation throughout FDA. Panels will discuss:

Patient Focused FDA Initiatives
Patient Engagement Opportunities
Addressing Challenges and Opportunities with AI Technology
Utilizing Real-World Data and Real-World Evidence at FDA

More info at https://www.fda.gov/news-events/fda-meetings-conferences-and-workshops/public-meeting-fda-rare-disease-day-2026-02232026

Around the World: Technological Frontiers in South American Gene and Cell Therapy
2025-12-16 10:00 - 11:00
As gene and cell therapies revolutionize modern medicine, South America is emerging as a dynamic player on the global stage—leveraging scientific innovation, regulatory evolution, and regional collaboration. This free virtual program explores the technological frontiers shaping the development and deployment of advanced therapies across the continent.
Webinar | Free

Breakthroughs in Targeted In Vivo Gene Editing
2025-11-20 - 2025-11-21
Join ASGCT at the Marriott Marquis San Diego Marina, Nov. 20-21, 2025, for an unparalleled opportunity to immerse yourself in cutting-edge solutions for targeted delivery of gene editing technology in vivo in San Diego. Hear from SCGE researchers Bill Peranteau, Sonia Vallabh, Yong-Hui Jiang, Kiran Musunuru, and Rebecca Ahrens-Nicklas at the event.
Virtual and In Person (San Diego, CA)
https://www.asgct.org/events/breakthroughs

Molecular Therapy Presents: Advancing AAV Technology
2025-10-22 10:00 - 11:00
“Advancing AAV Technology: From Capsid Design to Scalable Manufacturing” – An ASGCT Webinar
Virtual | Free

NORD® Rare Diseases and Orphan Products Breakthrough Summit
2025-10-20 - 2025-10-21
Shape the future of rare disease treatments, research and policy at the NORD® Rare Diseases and Orphan Products Breakthrough Summit.® Together, we can advance equity and innovation for the more than 30 million Americans – and more than 400 million people worldwide – with rare diseases!
Washington DC
nordsummit.org

Cell & Gene Therapy World Conference 2025
2025-09-10 - 2025-09-12
The Cell & Gene Therapy World Conference 2025 (CGTWC 2025), Boston, Massachusetts, USA, focuses on the vital progression of innovations and breakthroughs through cutting-edge research and practice in gene therapy for neurological disorders. Our aim is to explore new pathways in the field and bridge existing gaps in treatment options.
Boston, MA
https://www.cellgenetherapyconference.com/

Genome Engineering: CRISPR Frontiers
2025-08-12 - 2025-08-16
The specific goal for this meeting is to foster fruitful and creative interactions between researchers interested in applying these systems to genome engineering and related advances in a wide variety of organisms, together with scientists studying the basic biology of CRISPR-Cas and related bacterial defense systems. Hear from numerous SCGE researchers, including David Liu, Rebecca Ahrens-Nicklas, Ben Kleinstiver, Niren Murthy, and Jonathan Weissman.
Cold Spring Harbor Laboratory
https://meetings.cshl.edu/meetings.aspx?meet=CRISPR&year=25

Cell & Gene Therapy Summit 2025
2025-07-07 - 2025-07-09
We cordially invite you to The Global Cell & Gene Therapy Summit, which will be held in Orlando, FL, from July 07 to 09, 2025. Professionals and researchers are requested to take part as delegate, sponsor, or exhibitor. The three-day conference aims to bring together the global audience to discuss and exchange ideas on the origin, development, clinical applications and translation science of cell & gene therapy.
The inclusion of talks, poster presentation, workshops, discussions and networking events over the three days indicates a comprehensive program design to engage participants of various interactive formats. It allows the attendees to learn from experts, showcase their own research through posters, participate in workshops to gain practical insights, engage in discussions to share perspectives, and connect with professional researchers from diverse backgrounds.
By fostering such an environment, The Global Cell & Gene Therapy Summit, provides an excellent platform for researchers, clinicians, industry professionals, and other stakeholders to stay up to date with the latest advancements in the field of cell & gene therapy. It also facilitates collaboration and the exchange of knowledge, which is crucial for accelerating the translation of scientific discoveries into potential clinical applications.
Orlando, FL (Hybrid)
Learn more at https://cgtsummit.com/
