Somatic Cell Gene Editing

2023 Upconverting Nanoparticles Gordon Research Conference: Upconverting and Related Light-Conversion Materials Aimed at Biomedical, Energy and Quantum Applications
2023-06-17 - 2023-06-23 | Waterville Valley, 56 Packard's Road, Waterville Valley, NH, 03215, United States
The Upconverting Nanoparticles GRC is a premier, international scientific conference focused on advancing the frontiers of science through the presentation of cutting-edge and unpublished research, prioritizing time for discussion after each talk and fostering informal interactions among scientists of all career stages. The conference program includes a diverse range of speakers and discussion leaders from institutions and organizations worldwide, concentrating on the latest developments in the field. The conference is five days long and held in a remote location to increase the sense of camaraderie and create scientific communities, with lasting collaborations and friendships. In addition to premier talks, the conference has designated time for poster sessions from individuals of all career stages, and afternoon free time and communal meals allow for informal networking opportunities with leaders in the field.
Upconverting nanoparticles (UCNPs) and related frequency-conversion nanomaterials find themselves at the intersection of many of today’s most important and demanding research areas including deep-tissue bio-imaging, sensing, and theranostics; solar light harvesting; neuroscience and optogenetics; nanoscale thermometry; and quantum communication. The rapidly emerging insights into fundamental – and tunable – upconverting nanomaterials properties together with fast-growing application spaces provides an exciting opportunity for the scientific exchange of unpublished data and provocative ideas that will ultimately maximize impact in the biomedical, information technology, and energy sectors. The 2023 GRC on Upconverting Nanoparticles brings together biologists, materials scientists, chemists, physicists, engineers, and theory and computational experts. It will accelerate progress and address the core challenges in this far-reaching research area, uniting world-renowned senior and junior experts. Participants will experience cutting-edge and thought-provoking invited lectures and engage in extensive scientific discussions and interaction with researchers, students, and postdoctoral fellows. Each lecture will be followed by ample time for lively discussion and question-and-answer sessions among invited speakers, discussion leaders, and all participants.

2023 Polyamines Gordon Research Conference: Polyamines in Cancer, Medical Genetics, Aging, Pathogens and Plants
2023-06-24 - 2023-06-30 | Waterville Valley, 56 Packard's Road, Waterville Valley, NH, 03215, United States
The Polyamines GRC is a premier, international scientific conference focused on advancing the frontiers of science through the presentation of cutting-edge and unpublished research, prioritizing time for discussion after each talk and fostering informal interactions among scientists of all career stages. The conference program includes a diverse range of speakers and discussion leaders from institutions and organizations worldwide, concentrating on the latest developments in the field. The conference is five days long and held in a remote location to increase the sense of camaraderie and create scientific communities, with lasting collaborations and friendships. In addition to premier talks, the conference has designated time for poster sessions from individuals of all career stages, and afternoon free time and communal meals allow for informal networking opportunities with leaders in the field.
This 2023 GRC/GRS will focus on the role of polyamines and polyamine-associated pathways in humans, animal models, microorganisms, and plants. Speaker sessions will feature topics on adult and pediatric cancers, medical genetics, aging, pathogens, and plants. Speakers have been chosen to highlight the most recent discoveries related to the biological roles of polyamines and the important clinical trials investigating polyamine-based targeting therapies for the treatment and prevention of cancer, genetic abnormalities, neurodegenerative disorders, and microbial pathogens.

The Calcium and Cell Function Conference
2023-06-24 - 2023-06-30 | The Grand Hotel Malahide, Grove Rd, Malahide, K36 XT65, Ireland
The program will address the rapidly moving research on receptor-regulated calcium signaling and the critical questions that are key to establishing future therapies for cardiovascular, airway, gut, liver, immunoinflammatory, metabolic and neurological disorders. It is the only conference on this important topic that will be convened in 2023.
Conference sessions will present the latest findings and promote discussion on:
• Emerging new technologies to study calcium signaling
• Organellar calcium signaling
• Calcium signaling in metabolism and muscular and cardiovascular systems
• Store operated calcium channels and TRP channels
• Calcium signaling in cancer and the immune system
• Calcium signaling in the nervous system
• Calcium crosstalk with other signaling pathways
• Calcium signaling proteins and regulatory mechanisms
• New and notable session with latest breakthroughs
The conference covers 11 sessions, 33 speakers, 16 junior investigator talks, and four poster sessions. The program includes two Career Development Workshops: one for postdocs and early career scientists about funding opportunities and how to write a successful grant; and a roundtable discussion with individuals from academia, industry, and publishing on the topic of career paths.

The Biology & Chemistry of Vision Conference
2023-06-24 - 2023-06-29 | Loews Ventana Canyon Resort, 7000 North Resort Drive, Tucson, AZ, 85750, United States
Retinal photoreceptor cells provide the critical first steps in vision, transducing incident photons into changes in membrane potential relayed via neural circuits to higher visual centers. Research on photoreceptors and their supporting epithelium, the retinal pigment epithelium (RPE), is not only essential for understanding how we see, but it has also advanced knowledge in areas such as G protein signaling, neurophysiology, and protein structure and function.
In addition, fundamental photoreceptor and RPE research has been essential for new insights in the pathobiology of vision loss; blinding diseases like retinitis pigmentosa and macular degeneration result from photoreceptor degeneration that typically first appears as defects in cell biological and physiological mechanisms of the photoreceptors and/or the adjacent RPE.

Advancing Gene Therapy 2023
2023-06-25 - 2023-06-28 | The Westin Waltham Boston, 70 3rd Ave, Waltham, MA, 02451, United States
The 2023 Advancing Gene Therapy conference will be held in The Westin Walthum, MA. The meeting will provide conference attendees updates on recent gene therapy innovations from vector designs to product launch. Drivers of these advances will be discussed including the rapid pace of change from biotechnology, pharmaceutical, manufacturing and CROs with preclinical, non-clinical and trial expertise. In addition, the summit covers emerging and related fields including Gene Editing & CRISPR, Cell Therapies, Gene Therapy for Cancer, Immunotherapy, Rare diseases, Blood Disorders, Neurological Disorders, Toxicology Studies, advances in manufacturing, regulatory and medical affairs, Commercialization Strategies, Business Models and Market Access.

CRISPR 2023
2023-06-26 - 2023-07-01 | Julius-Maximilians-Universität Würzburg, Sanderring 2, Würzburg, 97070, Germany
The scientific program will cover various aspects of CRISPR biology ranging from genetics, biochemistry, structural biology, ecology, evolution and applications. The scientific part of the meeting is planned for June 28 to 30. We hope to welcome you in Würzburg June 27 at the evening reception. A group activity is being planned for July 1.

CMC Strategy Forum North America
2024-01-22
The CMC Strategy Forum is the premier scientific meeting that brings together regulatory, industry, and academic professionals to discuss key emerging CMC issues that affect biotechnology in an open and transparent workshop format.
Find more information at: https://www.casss.org/wcbp-cmc-north-america/cmc-north-america

Gene Therapy Regulatory Affairs
2024-01-23 - 2024-01-25
Overcome regulatory hurdles across non-clinical, clinical & CMC functions from pre-IND through to approval and satisfy regulatory requirements for gene therapies by demonstrating safety & efficacy.
Find more information at https://genetherapy-regulatory.com/

WCBP 2024
2024-01-23 - 2024-01-25
The WCBP Symposium is known as the highest-regarded annual conference addressing the role of current and emerging CMC analytical technology among evolving US and international regulatory perspectives. Hear from and engage with leaders on a wide range of topics including CMC development strategies, innovative analytical characterization, global submission strategies, next-generation therapeutics & vaccines, as well as the challenges and promises of CRISPR-based therapeutics. This year, WCBP will be co-sponsored by the US FDA.
Find more information at https://www.casss.org/wcbp-cmc-north-america/wcbp

Precision Medicine World Conference
2024-01-24 - 2024-01-26
PMWC brings together recognized leaders, top global researchers and medical professionals, and innovators across healthcare and biotechnology sectors to showcase practical content that helps close the knowledge gap between different sectors, thereby catalyzing cross-functional fertilization & collaboration in an effort to accelerate the development and spread of precision medicine.
For more information at: https://pmwcintl.com/

The State of Cell and Gene Therapy 2024
2024-01-24 10:00 - 15:30 (America/Chicago)
In this free virtual event, Genetic Engineering and Biotechnology News is bringing together people from industry and academia to discuss the latest research developments, innovations, and disruptive technologies that are impacting patients’ lives today and will spur cell and gene therapies bigger and better things tomorrow.
SCGE PI Kiran Musunuru will be speaking at the event. Find more details here: Event summary – Event Page | The State of Cell and Gene Therapy 2024 (liebertpub.com)

Gene Therapy Comparability Summit
2024-02-13 - 2024-02-15
The 4th Gene Therapy Comparability Summit will share the lessons learnt by biopharma directly dealing with comparability for their clinical-stage assets. Uniting the key stakeholders tackling comparability across regulatory, process development, CMC, and analytics departments, this summit will ensure that you can establish comparability in your clinical phase of development and prove to regulators that your products are comparable when scaling up for commercialization and navigating process changes.
Find more information at: https://genetherapy-comparability.com/

Rare Disease Day at NIH
2024-02-29
Rare Disease Day at NIH aims to raise awareness about rare diseases, the people they affect, and NIH collaborations that address scientific challenges and advance research for new treatments.
Find more information at https://ncats.nih.gov/news-events/events/rdd

The Allied Genetics Conference 2024
2024-03-06 - 2024-03-10
The Allied Genetics Conference (TAGC) is a unique conference organized by the Genetics Society of America that offers innovative sessions that get to the heart of our shared research interests. The diverse and interdisciplinary scope of TAGC 2024 allows researchers to discover answers and explore new directions in today’s genetics and genomics research.
Find more information at: https://genetics-gsa.org/tagc-2024/

Genomics of Rare Disease
2024-03-25 - 2024-03-27
The 18th conference on rare disease combines recent research on genetic mechanisms involved in disease, with advances in approaches for clinical care. This year’s conference will include discussions on the use of a ‘pangenome’ to improve diagnostic yield, the role of common variants in rare disease, and new developments in prenatal and neonatal genomic screening. This highly-interactive meeting fosters knowledge exchange among clinicians, clinical scientists, researchers and bioinformaticians working on rare diseases.
Find more information at: https://coursesandconferences.wellcomeconnectingscience.org/event/genomics-of-rare-disease-20240325/

Pharma USA 2024
2024-03-26 - 2024-03-27
Join pioneers from Commercial, Marketing, Medical Affairs, RWE, Market Access, Patient Engagement, and key stakeholders, will come together to deliver value to overcome the challenges that threaten the future viability of innovation.
Find more information at: https://events.reutersevents.com/pharma/pharma-usa

Gene Therapy for Rare Disorders
2024-03-26 - 2024-03-29
Bringing together key figures from industry, regulatory bodies, patient non-profits, payers, and key service providers, this is the field’s foremost meeting for collectively progressing rare gene therapy programs into and through the clinic.
Find more information at: https://genetherapy-conference.com/

Gene Therapy for Muscular Disorders
2024-04-16 - 2024-04-18
The 4th Gene Therapy for Muscular Disorders Summit in April will focus on gene therapies for muscular disorders to tackle the most pressing challenges and together, seek solutions to realize these novel therapeutic potentials for patients in need.

Learn more at https://genetherapy-muscular.com/

CRISPR and Beyond: Perturbations at Scale to Understand Genomes
2024-04-22 - 2024-04-24
The rapid development of CRISPR/Cas-based technologies makes it possible to modulate genomes with relative ease. These tools can help us understand how genetic variation influences phenotype and thereby answer long-standing questions in biology that impact human health, laying the foundations for precision medicine for heritable diseases and cancer treatment.
The 5th CRISPR and Beyond conference provides a forum for biomedical researchers from academia and industry working on high throughput screening, genome engineering, and variant effect interpretation to discuss perturbations at scale to understand genomes.
This year’s meeting will highlight recent advances enabled by emerging technologies and models, including computational approaches and designing DNA for function. Discussions will focus on the recent discoveries in precision genome editing, coding and non-coding variation and genetic interactions. A panel discussion will probe how generative modelling and other applications of machine learning are shaping the present and future of the field, and impacting experimentation.
Find more information at https://coursesandconferences.wellcomeconnectingscience.org/event/crispr-and-beyond-perturbations-at-scale-to-understand-genomes-20240422/

The CRISPR MEDiCiNE Conference
2024-04-23 - 2024-04-25
Meet the European CRISPR Medicine and Genomic Medicine community to discuss tools, delivery, safety, functional genomics, standards and regulations, and more.
Find more information: https://crisprmedicinenews.com/crisprmed24/

Rare Drug Development Symposium
2024-04-29 - 2024-05-01
The RARE Drug Development Symposium, hosted by Global Genes and the Orphan Disease Center of the University of Pennsylvania, equips advocates with the knowledge, skills and connections they need to advance therapy development for their communities.
Find more information at: https://www.globalgenes.org/event/rare-disease-drug-development/

ASGCT Annual Meeting
2024-05-07 - 2024-05-11
The American Society of Gene and Cell Therapy’s (ASGCT) Annual Meeting is the premier event for professionals in gene and cell therapy to learn from the latest scientific research, stay up to date on new technologies, and make career-advancing connections with peers.
Learn more at https://annualmeeting.asgct.org/
Want to see the SCGE’s involvement in ASGCT 2024? Click here.

Natural History Studies and Registries in the Development of Rare Disease Treatments
2024-05-13 09:00 - 15:00
This in-person and virtual public workshop will bring together rare disease patient advocates, academic researchers, regulated industry, and other key stakeholders to discuss considerations for the use of natural history study and registry data in rare disease drug development programs.
Find more information at https://reaganudall.org/news-and-events/events/natural-history-studies-and-registries-development-rare-disease-treatments

International Society for Cell & Gene Therapy
2024-05-28 - 2024-06-01
Address obstacles at each stage of translation and progress the future of cell and gene therapies to bring scientific innovation to therapeutic reality for patients worldwide.
Vancouver, Canada
Learn more at https://www.isctglobal.org/isct2024/home

Gene Therapy Patient Engagaement
2024-05-29 - 2024-05-31
Join 80+ patient advocacy and engagement professionals at gene therapy companies and patient advocacy groups to gain actionable insights that you can immediately implement into your own gene therapy programs, and come together with the community to develop solutions to the challenges that are unique to the gene therapy space.
Boston, MA
https://genetherapy-patient-engagement.com/

2024 Regulatory Education for Industry
2024-05-29 - 2024-05-30
Learn directly from the FDA’s regulatory experts in medical product centers: drugs, devices, and biologics. This course is designed to provide participants with a strong, basic foundation in the FDA’s regulatory requirements, and also create awareness of current activities. Attend virtually or in-person.

REdI Annual Conference 2024

The State of CRISPR and Gene Editing
2024-06-05 10:00 - 14:30
In The State of CRISPR and Gene Editing virtual summit, GEN proudly gathers a tantalizing line-up of luminaries from academia and industry to discuss the latest research developments, innovations, and advanced technologies that are expanding the CRISPR toolbox, delivering new therapies to patients and safeguarding our food supply. The webinar is virtual and free to attend. SCGE Researcher David Liu will be giving the opening keynote.

Learn more at https://webinars.liebertpub.com/e/the-state-of-crispr-and-gene-editing-2024

Cell and Gene Therapy Products Symposium
2024-06-11 - 2024-06-13
The Cell and Gene Therapy Products (CGTP) Symposium: Manufacturing, Quality and Regulatory Considerations enables the exchange of scientific ideas and dialogue with regulators that form the basis of evolving regulatory practices in the development of these diverse and innovative products.
Rockville, MD
https://www.casss.org/cell-gene-therapy-products

Next Generation Gene Therapy Vectors
2024-06-12 - 2024-06-14
This event will focus on finding and optimizing novel vectors to increase specificity, target new cell types, expand packaging capacities, and reduce toxicity risks to create safer, cost-effective and efficacious gene therapies.
Learn more at https://next-gen-genetherapy-vectors.com/

Genome Engineering: Research and Applications
2024-06-16 - 2024-06-20
The conference seeks to present the latest research findings in these fields and support early-career investigators, women, and other historically-excluded groups in the field of genome editing. Through collaboration and networking at this meeting, it can accelerate the translation of fundamental advances into viable genome editing technologies. The conference is being held in Rome, Italy.
SCGE researcher Shengdar Tsai is one of the conference organizers, and SCGE researcher David Liu is the keynote speaker.
Learn more at https://events.faseb.org/event/genome-engineering-research-applications/summary
