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Clinical Trial Report

Gene Therapy Trial Report

Summary

Safety and Efficacy of a Single Subretinal Injection of JWK002 Gene Therapy in Subjects With X-linked Retinoschisis(XLRS)


NCTID NCT06345898 (View at clinicaltrials.gov)
Description
Indication Retinoschisis, X-linked
Compound Name JWK002
Sponsor West China Hospital
Funder Type Other
Status
Recruiting
Enrollment Count 18

Therapy Information


Target Gene/Variant RS1
Therapy Type Gene transfer
Therapy Route In-vivo
Mechanism of Action Functional gene replacement
Route of Administration Subretinal
Drug Product Type Viral vector
Target Tissue/Cell
Delivery System Viral transduction
Vector Type AAV8
Editor Type
Dose 1 Undisclosed low dose
Dose 2 Undisclosed medium dose
Dose 3 Undisclosed high dose
Dose 4
Dose 5

Study Record Dates


Current Stage Early phase1
Submit Date 2024-03-28
Completion Date 2029-12-30
Last Update 2024-07-23

Participation Criteria


Eligible Age 5 Years - 18 Years
Standard Ages Child, Adult
Eligible Sex MALE

Locations


No.of Trial Sites 1
Locations China

Regulatory Information


Has US IND False
Recent Updates Investigator-initiated trial conducted at West China Hospital

Resources/Links


Resources/Links

No External Links Available.