SCGE Public Workshop

The SCGE is hosting a public workshop titled “Rethinking Clinical Delivery, Regulation, and Payment Models for Individualized Platform-Based Genome Editing Therapies”.

The workshop is on Tuesday, September 29th, 2026. You can register to attend this event virtually at the button below.

Meet the Expert: Shyam Patel, Kevin Strauss, Manar Zaghlula

Meet the Expert: Jessica Chaikof, Rachel Chaikof, and Stacey Ashlund

In this video of the SCGE Meet the Expert series, panelists provide patient and caregiver perspectives on gene therapy for hearing and vision loss.

SCGE Comment on Plausible Mechanism Framework

SCGE Investigational New Drug (IND) Application Toolkit for Gene Therapy

The TCDC has created a collection of useful resources, templates, and tools for filling out an IND application. Find these free, public resources at the link below. 

Program Snapshot

The goal of the SCGE program is to accelerate the development of genome editing therapies into the clinic. For Phase 2, there are four program initiatives:

1. Developing technologies and assays for safety and efficacy studies
2. Optimizing genome editing-based therapeutic leads to support advancement towards clinical trials
3. Supporting novel genome editing clinical trials for more than one disease
4. Fostering collaboration and sharing new technologies and protocols with the public and research community

For ethical, legal, and safety reasons, the SCGE program does NOT support any research activities on genome editing in reproductive (germ) cells.

Learn more about individual and collaborative research projects, as well as the SCGE program and deliverables, below: