Publication Title | Journal | Authors | Pub Date | PubMed | Project PIs |
---|---|---|---|---|---|
Efficient in vivo prime editing corrects the most frequent phenylketonuria variant, associated with high unmet medical need | American Journal of Human Genetics | Brooks et al. | 11/3/23 | 37924808 | Peranteau, Musunuru |
A base editing strategy using mRNA-LNPs for in vivo correction of the most frequent phenylketonuria variant | HGG Advances | Brooks et al. | 10/31/23 | 37922902 | Peranteau, Musunuru |
Phase 2 PublicationsAllison Zappa2023-11-09T10:51:06-06:00