The American Society of Gene and Cell Therapy’s (ASGCT) Annual Meeting is the premier event for professionals in gene and cell therapy to learn from the latest scientific research, stay up to date on new technologies, and make career-advancing connections with peers. Many members in the SCGE consortium attend and present at the event. Learn more about SCGE investigator involvement below:

Blue boxes denote oral presentations, gray boxes denote posters, red boxes denote Keynote presentations

Tuesday May 13th

Steve Gray, “Unique considerations with rare disease”

8:30 am, Room 291-292

Beverly Davidson, “Proof of direct benefit through nonclinical pharmacology”

8:00 am – 12:00 pm, NOLA A

Allyson Berent, “A model for a mature non-profit”

11:15 am, NOLA Theater A

Scientific Symposium, “Who’s Afraid Of Off-Target Editing? A Discussion Of Hypothetical Risks In The Context Of Known Genotoxic Medical Interventions”

1:30-3:15, Room 293-296

Chairs: PJ Brooks, Claire Clelland

Claire Clelland, “Framework for assessing genomic off-targets of CRISPR gene editing therapies in a clinical context”

1:30 pm, Room 293-296

Petros Giannikopoulos, “Case example: Ionizing radiation for childhood medulloblastoma”

1:55 pm, Room 293-296

Kris Saha, “Patient perspectives on gene editing and off-target editing”

2:20 pm, Room 293-296

Kiran Musunuru, “Framework for considering which off-target edits are of concern”

2:45 pm, Room 293-296

Wednesday May 14th

Fyodor Urnov, “General Overview of Combining Tech”

8:00 am, Room 291-292

Rebecca Ahrens-Nicklas, “Investigators guide to identifying and validating biomarkers for clinical trials”

8:00 am, Room 265-268

Drew Weissman, “Nucleoside-modified mRNA-LNP Therapeutics”

10:15 am, Hall F

*Keynote Presentation

Allyson Berent, “Understanding patients’ and caregivers’ lives and needs”

3:45 pm, Room 293-296

Thursday May 15th

Fyodor Urnov, “Overview of therapeutic genetic modalities for CNS disease treatment”

8:00 am, Room 293-296

Zheng-Yi Chen, “Dual AAV vectors, clinical trial data for hearing loss”

8:25 am, NOLA Theater B

Kiran Musunuru, “Therapeutic Gene Editing for Cardiovascular and Metabolic Diseases: From the Leading Cause of Death to N-of-1 Disorders”

10:15 am, Hall F

*Keynote Presentation

Friday May 16th

Steve Gray, “Transgene regulation strategies for dose-sensitive genes involved with neurodevelopmental disorders”

8:00 am, Room 291-292

Allyson Berent, “Translating Clinical Developments for Families and Patients with Rare Diseases”

8:25 am, Room 388-390

Benjamin Deverman, “Utilizing AI in Academic Labs”

1:30 pm, Room 293-296

Saturday May 17th