Manda Arbab

Manda Arbab, PhD, is an Assistant Professor at the Translational Neuroscience Center at Boston Children’s Hospital and Harvard Medical School Department of Neurology. She is a PI on the SCGE Phase 2 U19 project titled “Preclinical Genome Editing for Rare Neurological Diseases“.

In this interview, Dr. Arbab discusses her research on translating a base editing strategy for patients with Spinal Muscular Atrophy (SMA), and her excitement about working in the gene editing field during a time where there are rapid advancements happening.