A large number of long non-coding RNAs (lncRNAs) with a surprisingly wide-range of cell-type specific expression profiles are present in human transcriptomes. Emerging evidence points to their critical roles in human physiology and pathology and some are recognized as potential therapeutic targets. However, many seminal questions in regard to their mechanism of action remain largely unexplored.

ASGCT 24th Annual Meeting Join Jennifer Doudna, Ph.D., for a Fireside Chat

Usher 1F Collaborative is pleased to announce our scientific research conference, Therapeutic Strategies for Large Protein Coding Genes in Usher Syndrome.