This Scientific Exchange with the FDA seeks to make progress on therapeutic development for rare conditions that are scientifically feasible but commercially non-viable.

The Reagan-Udall Foundation for the FDA, in collaboration with the Food and Drug Administration (FDA), is hosting a public webinar as part of a series of webinars for FDA-issued guidance related to real-world evidence (RWE). This latest session in the webinar series will discuss the draft guidance: Integrating Randomized Controlled Trials for Drug and Biological Products Into Routine Clinical Practice.

This free, public event will explore key immunology-related topics that have implications across the class of AAV gene therapies, including immune responses, antibody testing, and redosing strategies.

Stay tuned for more details

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Explore cutting-edge advancements in the use of AAV vectors for [...]

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Human Genetics and Genetical Disorders-2025 extend our immense pleasure and honor [...]

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The Festival is designed principally for scientists and clinicians who are [...]

This webinar will consider patient-centered approaches in the specific context [...]

We cordially invite you to The Global Cell & Gene [...]

The specific goal for this meeting is to foster fruitful [...]

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Shape the future of rare disease treatments, research and policy [...]

"Advancing AAV Technology: From Capsid Design to Scalable Manufacturing" - [...]

Join ASGCT at the Marriott Marquis San Diego Marina, Nov. [...]

This free, virtual summit from ASGCT will bring together patients, [...]

International Society for Cell & Gene Therapy 2026 Annual Meeting [...]

Boston, MA or Virtual https://annualmeeting.asgct.org/