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ExperimentGene editing in vitro by various peptide variants delivering Cas RNPs to primary Human airway epithelia cells.
Experiment ConditionS10, Cas12a, CFTR
Assay Description: Calculated editing efficiency mean of 3 biological replicates by sanger sequencing.
Tissue Measured:
Measurement Type:Editing Efficiency
Record ID15000000535

EditorAsCas12a (Feldan Therapeutics)
Delivery SystemS10
Delivery System SubtypeAmphiphilic peptide
Guideg-45_C12a
Vector

Model SpeciesHuman
Model NamePrimary Airway Epithelia

Application MethodIn Media
Application Site
Dosage1.33uM Cas12a/2.0uM gRNA/40uM Shuttle Peptide
Injection Frequency
Injection Rate
Injection Volume
Days post injection72 hours
Editor FormatRNP
Antidote Id
Antidote Description

Measured Values
Samples Size: 1
 
Replicate Result (Editing Efficiency)
Measurement Units: % indel
Mean 26.00 
1 26.0 
  

Publication Title
Engineered amphiphilic peptides enable delivery of proteins and CRISPR-associated nucleases to airway epithelia. NCBI