SCGE ID10000000396
Lab IDJCR183
SourceAAV encoded (see vector details)
Target LocusDMD
Specieshuman/rhesus
Descriptionguide targeting an intronic seqeunce within the Rhesus and human DMD gene
Guide CompatibilitySaCas9

Target SequenceAGAACTGGTGGGAAATGGTCTAG
Target Sequence + PAMAGAACTGGTGGGAAATGGTCTAGGAGAGT
PositionrheMac10/X:31680639-31680661

Spacer SequenceAGAACUGGUGGGAAAUGGUCUAG
Spacer Length23
Modificationsnone

  • SaCas9



  • This Guide: JCR183 is being used ...
    Project Initiative Contact PI
    Delivery Systems Aravind Asokan, PhD
    (Duke University)
    NIH Report