SCGE ID14000000104
NameAAVcc47-SaCas9/guide DMD
DescriptionAll-in-one vector casette (CMV-saCas9-U6-gRNA [human/rhesus DMD intron])
TypeViral Vector
SubtypeAAV

SourceAsokan/Gersbach Labs

Genome SerotypeAAV2
Capsid SerotypeAAV.cc47
Capsid Variant452-GVSLGGG-458
Stock/Catalog/RRID

Annotated MapFilename: pt366-aav-cmv-nls-sacas9-nls-3xha-bghpa-u6-jcr183_human-dmd.gb
Titer MethodqPCR


This Vector/Format: AAVcc47-SaCas9/guide DMD is being used ...
Project Initiative Contact PI
Delivery Systems Aravind Asokan, PhD
(Duke University)
NIH Report