| Peptide Shuttle optimization to deliver Cas12a RNP to human airway epithelia cells |
| FSD301 |
| Calculated editing efficiency by % of NGS reads that showed an indel |
|
| Editing Efficiency |
| 15000000884 |
|
| AsCas12a (Feldan Therapeutics) |
| FSD301 |
| Amphiphilic peptide |
| 3849 45-5' |
|
|
| Human |
| Primary Airway Epithelia |
|
|
|
| 2uM gRNA, 1.33uM Cas12a, 40uM Shuttle |
|
|
|
|
| ribonucleoprotein (RNP) |
|
|
|
| Measured Values |
| Samples Size: | 5 |
| |
| Mean |
25.79  |
| 1 |
31.33  |
| 2 |
25.17  |
| 3 |
27.63  |
| 4 |
22.18  |
| 5 |
22.66  |
| |
|