| Peptide Shuttle optimization to deliver Cas12a RNP to human airway epithelia cells |
| FSD304 |
| Calculated editing efficiency by % of NGS reads that showed an indel |
|
| Editing Efficiency |
| 15000000886 |
|
| AsCas12a (Feldan Therapeutics) |
| FSD304 |
| Amphiphilic peptide |
| 3849 45-5' |
|
|
| Human |
| Primary Airway Epithelia |
|
|
|
| 2uM gRNA, 1.33uM Cas12a, 40uM Shuttle |
|
|
|
|
| ribonucleoprotein (RNP) |
|
|
|
| Measured Values |
| Samples Size: | 6 |
| |
| Mean |
20.64  |
| 1 |
13.49  |
| 2 |
13.84  |
| 3 |
23.45  |
| 4 |
30.95  |
| 5 |
24.96  |
| 6 |
17.12  |
| |
|