| Peptide Shuttle optimization to deliver Cas12a RNP to human airway epithelia cells |
| FSD306 |
| Calculated editing efficiency by % of NGS reads that showed an indel |
|
| Editing Efficiency |
| 15000000888 |
|
| AsCas12a (Feldan Therapeutics) |
| FSD306 |
| Amphiphilic peptide |
| 3849 45-5' |
|
|
| Human |
| Primary Airway Epithelia |
|
|
|
| 2uM gRNA, 1.33uM Cas12a, 40uM Shuttle |
|
|
|
|
| ribonucleoprotein (RNP) |
|
|
|
| Measured Values |
| Samples Size: | 3 |
| |
| Mean |
3.87  |
| 1 |
4.07  |
| 2 |
3.54  |
| 3 |
4  |
| |
|