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ExperimentIndependent validation for Asokan Delivery Team: Evolving High Potency AAV Vectors for Neuromuscular Genome Editing.
Experiment ConditionSaline Neg control, Male
Assay Description: Editing efficiency calculated by counting fluorescent cells (RFP) compared to DAPI stained nuclei
Tissue Measured:heart
Cell Type :cardiac muscle cell
Measurement Type:Editing Efficiency
Record ID15000001297

Editor
Delivery System
Delivery System Subtype
Guide
Vector

Model SpeciesMouse
Model NameB6.Cg-Gt(ROSA)26Sor ^ tm9(CAG-tdTomato)Hze/J

Sample SexMale

Application Methodintravenous, tail vein
Application Siteliver and heart
Dosage
Injection Frequencyonce
Injection Rate
Injection Volume200 microliters
Days post injection4 weeks
Editor Format
Antidote Id
Antidote Description

Measured Values
Samples Size: 2
 
Replicate Result (Editing Efficiency)
Measurement Units: Signal
Mean 2 of 2 No red cells 
1 No red cells 
2 No red cells 
  

Title Description File Download SCGE ID
Heaney_SATC Tissue Processing, Imaging and Analysis Procedure for tissue preparation, imaging and analysis. Heaney_SATC_Tissue_Processing_Imaging_and_Analysis.pdf 21000000025