| 
        
            
            | Independent validation for Asokan Delivery Team: Evolving High Potency AAV Vectors for Neuromuscular Genome Editing. |  | Saline Neg control, Female |  
                | Editing efficiency calculated by counting fluorescent cells (RFP) compared to DAPI stained nuclei |  
                | liver |  
                | hepatocyte |  
                | Editing Efficiency |  | 15000001298 |  | 
 |  |  |  |  |  |  |  |  |  |  |  | 
 |  | Mouse |  | B6.Cg-Gt(ROSA)26Sor ^ tm9(CAG-tdTomato)Hze/J |  | 
 |  | Female |  | 
 |  | intravenous, tail vein |  | liver and heart |  |  |  | once |  |  |  | 200 microliters |  | 4 weeks |  |  |  |  |  |  |  | 
 |  
                | Measured Values |  
                | Samples Size: | 2 |  |  |  
                
                
             
                 
                     
                     
                      
                
                | Mean | 2 of 2 No red cells  |  
                
                | 1 | No red cells  |  
                
                | 2 | No red cells  |  |  |  |