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ExperimentLarge animal testing of AAV9 vs AAVcc47 (Asokan lab's novel capsid) via intravenous administration to rhesus macaques
Experiment ConditionAAV9
Assay Description:
Tissue Measured:heart
Measurement Type:Delivery Efficiency
Record ID15000005720

EditorSaCas9
Delivery SystemAAV
Delivery System SubtypeViral vector
GuideJCR183
VectorAAV9-SaCas9/guide DMD;

Model Species
Model Name

Sample Age~3-4 months of age

Application Methodintravenous
Application Sitesystemic
Dosage1. 3e13vg/kg (1~1.5kg body weight)
Injection FrequencyOnce
Injection Rate
Injection Volume~1-2 ml
Days post injection4 weeks
Editor FormatAAV encoded
Antidote Id
Antidote Description

Measured Values
Samples Size: 3
 
Replicate Result (Delivery Efficiency)
Measurement Units: SaCas9/globin copies
Mean 1336.67 
1 1253 
2 1527 
3 1230