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ExperimentCre Recombinase dose escalation study in Ai9 mice
Experiment ConditionAAV9-CMV-Cre, 1e12vg, Male
Assay Description: Delivery efficency was calculated by measuring fluorescent intensity in tdTomato+ cells from multiple images and sections in liver, heart, skeletal muscle
Tissue Measured:skeletal muscle tissue
Measurement Type:Delivery Efficiency
Record ID15000000957

EditorCre recombinase
Delivery SystemAAV
Delivery System SubtypeViral vector
Guide
VectorAAV9-CMV-Cre;

Model SpeciesMouse
Model NameB6.Cg-Gt(ROSA)26Sor ^ tm9(CAG-tdTomato)Hze/J

Sample SexMale

Application Methodintravenous
Application Siteliver and heart
Dosage1e12vg
Injection Frequencyonce
Injection Rate
Injection Volume200 microliters
Days post injection4 weeks
Editor FormatAAV vector encoded
Antidote Id
Antidote Description

Measured Values
Samples Size: 1
 
Replicate Result (Delivery Efficiency)
Measurement Units: Corrected total cell fluorescence
Mean 1011925618 
1 1011925618 
  

Publication Title
Cross-species evolution of a highly potent AAV variant for therapeutic gene transfer and genome editing. NCBI
Cross-species evolution of a highly potent AAV variant for therapeutic gene transfer and genome editing. NCBI