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ExperimentLarge animal testing of AAV9 vs AAVcc47 (Asokan lab's novel capsid) via intramuscular administration to rhesus macaques
Experiment ConditionAAVcc47
Assay Description:
Tissue Measured:inguinal fat pad
Measurement Type:Delivery Efficiency
Record ID15000005729

EditorSaCas9
Delivery System
Delivery System Subtype
GuideJCR183
VectorAAVcc47-SaCas9/guide DMD;

Model Species
Model Name

Sample Age~3-4 months of age

Application Methodintramuscular
Application Siteleft quadriceps
Dosage3e13vg/NHP dose injected in the quad
Injection FrequencyOnce
Injection Rate
Injection Volume~1-2 ml
Days post injection4 weeks
Editor FormatAAV encoded
Antidote Id
Antidote Description

Measured Values
Samples Size: 4
 
Replicate Result (Delivery Efficiency)
Measurement Units: SaCas9/globin copies
Mean 24891 
1 12900 
2 83988 
3 2676 
4