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ExperimentRepeat experiment of independent validation of Chen delivery platform using LNPs to deliver CRISPR/Cas9 to mouse inner ear
Experiment ConditionControl
Assay Description: On-target editing analyzed by confocal imaging of whole mouse cochlea of direct fluorescence RFP (tdTomato) compared to Hoeschst stained nuclei.
Tissue Measured:scala tympani
Measurement Type:Editing Efficiency
Record ID15000003293

Editor
Delivery System306-O12B blank
Delivery System SubtypeNanoparticle
Guide
Vector

Model SpeciesMouse
Model NameB6.Cg-Gt(ROSA)26Sor^tm14(CAG-tdTomato)Hze/J

Sample SexMale

Application Methodcanalostomy injection
Application Siteinner ear
Dosage
Injection Frequencyonce
Injection Rate
Injection Volume1 microliter
Days post injection6 days
Editor FormatLipid Nanoparticle
Antidote Id
Antidote Description

Measured Values
Samples Size: 2
 
Replicate Result (Editing Efficiency)
Measurement Units: Signal
Mean 0 of 2 present 
1 absent 
2 absent