Experiment: Pcsk9 adenine base editor efficiency in liver and nonliver tissue
PI: Elliot L. Chaikof, MD, PhD
Description: Adenine base editing at the Pcsk9 exon 1 splice donor site in mouse heart, kidney, liver, lungs, muscle, and spleen was assessed one week after systemic administration of an adenine base editor delivered by engineered virus-like particles (BE-eVLPs) in C56BL/6 mice
Editing Assay:
adenine base editing at target Pcsk9 site in liver vs. other mouse organs (heart, kidney, lung, muscle, spleen)
Parent Project: Delivery Technologies for In Vivo Genome Editing
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Other experiments in this project: 1
Download: Submitted files
Publications:
Engineered virus-like particles for efficient in vivo delivery of therapeutic proteins. NCBI
Organ System Overview
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